Resource Overview:
Adeno-associated virus (AAV) vectors are the leading platform for gene therapy, offering safety, efficiency, and long-term expression without integrating into the genome. This resource explains what AAV vectors are, why they matter, and how characterization ensures purity, potency, and regulatory compliance. Learn the critical steps —from production and purification to analytics—that guarantee high-quality AAV for therapeutic applications.
Key Takeaways:
- AAV vectors are the leading platform for gene therapy due to safety and efficiency.
- Characterization ensures purity, potency, and regulatory compliance.
- Critical steps include production, purification, and analytical testing.
- Techniques like qPCR, BLI, and SDS-PAGE assess quality attributes.
- Comprehensive testing mitigates risks and supports clinical success.
Resource Details:
- Document type: Infographic
- Page count: 1
- Read time: 4 minutes